Extracellular vesicle-mediated gene editing for the treatment of nonsyndromic progressive hearing loss in adult mice.

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Title: Extracellular vesicle-mediated gene editing for the treatment of nonsyndromic progressive hearing loss in adult mice.
Authors: Pan X; College of Pharmacy, Department of Pharmaceutics, University of Florida, Gainesville, FL 32611, USA., Huang P; Department of Otolaryngology, Head and Neck Surgery, University of Kansas School of Medicine, Kansas City, KS 66160, USA., Ali SS; College of Pharmacy, Department of Pharmaceutics, University of Florida, Gainesville, FL 32611, USA., Renslo B; Department of Otolaryngology, Head and Neck Surgery, University of Kansas School of Medicine, Kansas City, KS 66160, USA., Greenberg Z; College of Pharmacy, Department of Pharmaceutics, University of Florida, Gainesville, FL 32611, USA., Erwin N; College of Pharmacy, Department of Pharmaceutics, University of Florida, Gainesville, FL 32611, USA., Li Y; Department of Medicinal Chemistry, Center for Natural Products, Drug Discovery, and Development, University of Florida, Gainesville, FL 32610, USA., Ding Z; College of Pharmacy, Department of Pharmaceutics, University of Florida, Gainesville, FL 32611, USA., Hutchinson TE; College of Pharmacy, Department of Pharmaceutics, University of Florida, Gainesville, FL 32611, USA., Warnecke A; Department of Otolaryngology, Hannover Medical School, 30625 Hannover, Germany., Fernandez NE; College of Pharmacy, Department of Pharmaceutics, University of Florida, Gainesville, FL 32611, USA., Staecker H; Department of Otolaryngology, Head and Neck Surgery, University of Kansas School of Medicine, Kansas City, KS 66160, USA., He M; College of Pharmacy, Department of Pharmaceutics, University of Florida, Gainesville, FL 32611, USA.
Source: Science translational medicine [Sci Transl Med] 2025 Nov 12; Vol. 17 (824), pp. eadn3993. Date of Electronic Publication: 2025 Nov 12.
Publication Type: Journal Article
Journal Info: Publisher: American Association for the Advancement of Science Country of Publication: United States NLM ID: 101505086 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1946-6242 (Electronic) Linking ISSN: 19466234 NLM ISO Abbreviation: Sci Transl Med Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:1946-6242
DOI:10.1126/scitranslmed.adn3993