| Authors: |
Brands MM; Department of Pediatrics, Division of Metabolic Diseases, Emma Children's Hospital, Amsterdam Gastroenterology Endocrinology Metabolism, Amsterdam UMC location University of Amsterdam, Amsterdam, The Netherlands., de Puyraimond C; Department of Pediatrics, Reference Center for Inborn Errors of Metabolism, Necker Hospital, APHP, Université Paris-Cité, G2m Network, MetabERN, Paris, France., Gospe SM Jr; Departments of Neurology and Pediatrics, University of Washington, Seattle, Washington, United States.; Department of Pediatrics, Duke University, Durham, North Carolina, United States., Schiff MM; Department of Pediatrics, Reference Center for Inborn Errors of Metabolism, Necker Hospital, APHP, Université Paris-Cité, G2m Network, MetabERN, Paris, France.; INSERM UMR _S1163, Institut Imagine, Université Paris-Cité, Paris, France., Jaeger B; Department of Child Neurology, Emma's Children's Hospital, Amsterdam UMC, Amsterdam, The Netherlands., Koot BG; Department of Pediatric Gastroenterology and Nutrition, Emma Children's Hospital, Amsterdam University Medical Centers, Location Academic Medical Center, University of Amsterdam, Netherlands., Raphael MF; Department of Pediatric Oncology, Emma Children's Hospital, Amsterdam UMC Location University of Amsterdam, Amsterdam, The Netherlands., Lubout CM; Department of Metabolic Diseases, Beatrix Children's Hospital, University Medical Center Groningen, University of Groningen, Groningen, the Netherlands., Soto B; Department of Pediatrics, CH Auxerre, Auxerre, France., Delanne J; Department of Genetics, CHU Dijon Bourgogne, Dijon, France., Imbard A; Department of Biochemistry, Hôpital Necker-Enfants Malades, APHP, Paris, France.; Département Médicaments et Technologies pour La Santé (DMTS), Paris-Saclay University, CEA, Gif-sur-Yvette, France., Zempel J; Departments of Neurology and Pediatrics, Washington University, St. Louis, Missouri, United States., Kraal KC; Princess Máxima Center for Pediatric Oncology, Utrecht, The Netherlands., Scheenstra R; Division of Pediatric Gastroenterology and Hepatology, Department of Pediatrics, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands., Clayton PT; Inborn Errors of Metabolism, Genetics and Genomic Medicine, UCL Great Ormond Street Institute of Child Health, London, United Kingdom. |