Base Editing of HBG1 and HBG2 Promoters for Sickle Cell Disease.

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Bibliographic Details
Title: Base Editing of HBG1 and HBG2 Promoters for Sickle Cell Disease.
Authors: Gupta AO; University of Minnesota, Minneapolis., Sharma A; St. Jude Children's Research Hospital, Memphis, TN., Frangoul H; Sarah Cannon Research Institute, Nashville.; TriStar Centennial Children's Hospital, Nashville., Kanter J; University of Alabama at Birmingham, Birmingham., Mapara MY; Columbia University Medical Center, New York., Dalal J; Rainbow Babies and Children's Hospital, Cleveland., Alavi A; Henry Ford Health System, Detroit., Jaroscak JJ; Medical University of South Carolina, Charleston., Ayala E; Mayo Clinic, Jacksonville, FL., DiPersio JF; Washington University, St. Louis., Ziga ED; University of Miami, Miami., Eapen M; Medical College of Wisconsin, Milwaukee., Rifkin-Zenenberg S; Hackensack University Medical Center, Hackensack, NJ., Minella AC; Beam Therapeutics, Cambridge, MA., Chen Y; Beam Therapeutics, Cambridge, MA., Chesler S; Beam Therapeutics, Cambridge, MA., Ambati S; Beam Therapeutics, Cambridge, MA., Bowman TS; Beam Therapeutics, Cambridge, MA., Habtemariam B; Beam Therapeutics, Cambridge, MA., Joseney-Antoine M; Beam Therapeutics, Cambridge, MA., Chockalingam PS; Beam Therapeutics, Cambridge, MA., Lin L; Beam Therapeutics, Cambridge, MA., Goyal S; Beam Therapeutics, Cambridge, MA., Simon A; Beam Therapeutics, Cambridge, MA., Thompson AA; Children's Hospital of Philadelphia, Philadelphia., Heeney MM; Dana-Farber/Boston Children's Cancer and Blood Disorders Center, Boston.
Corporate Authors: BEACON Investigators
Source: The New England journal of medicine [N Engl J Med] 2026 May 07; Vol. 394 (18), pp. 1824-1835. Date of Electronic Publication: 2026 Apr 01.
Publication Type: Journal Article; Clinical Trial, Phase I; Clinical Trial, Phase II; Multicenter Study
Journal Info: Publisher: Massachusetts Medical Society Country of Publication: United States NLM ID: 0255562 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1533-4406 (Electronic) Linking ISSN: 00284793 NLM ISO Abbreviation: N Engl J Med Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1533-4406
DOI:10.1056/NEJMoa2504835