Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD.
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| Title: | Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD. |
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| Authors: | Malecova B; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Sala D; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Melikian GM; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Johns R; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Erdogan G; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Hartmann M; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Jordan M; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Arias JD; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Bhattacharya A; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Meng Q; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Dansereau O; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Beppler SW; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Doppalapudi VR; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Huang H; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Flanagan WM; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Levin AA; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA. |
| Source: | Nucleic acids research [Nucleic Acids Res] 2026 Apr 13; Vol. 54 (7). |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Oxford University Press Country of Publication: England NLM ID: 0411011 Publication Model: Print Cited Medium: Internet ISSN: 1362-4962 (Electronic) Linking ISSN: 03051048 NLM ISO Abbreviation: Nucleic Acids Res Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 1362-4962 |
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| DOI: | 10.1093/nar/gkag301 |