Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD.
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| Title: | Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD. |
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| Authors: | Malecova B; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Sala D; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Melikian GM; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Johns R; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Erdogan G; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Hartmann M; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Jordan M; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Arias JD; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Bhattacharya A; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Meng Q; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Dansereau O; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Beppler SW; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Doppalapudi VR; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Huang H; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Flanagan WM; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Levin AA; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA. |
| Source: | Nucleic acids research [Nucleic Acids Res] 2026 Apr 13; Vol. 54 (7). |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Oxford University Press Country of Publication: England NLM ID: 0411011 Publication Model: Print Cited Medium: Internet ISSN: 1362-4962 (Electronic) Linking ISSN: 03051048 NLM ISO Abbreviation: Nucleic Acids Res Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 41994867 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Malecova+B%22">Malecova B</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Sala+D%22">Sala D</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Melikian+GM%22">Melikian GM</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Johns+R%22">Johns R</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Erdogan+G%22">Erdogan G</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Hartmann+M%22">Hartmann M</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Jordan+M%22">Jordan M</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Arias+JD%22">Arias JD</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Bhattacharya+A%22">Bhattacharya A</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Meng+Q%22">Meng Q</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Dansereau+O%22">Dansereau O</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Beppler+SW%22">Beppler SW</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Doppalapudi+VR%22">Doppalapudi VR</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Huang+H%22">Huang H</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Flanagan+WM%22">Flanagan WM</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Levin+AA%22">Levin AA</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%220411011%22">Nucleic acids research</searchLink> [Nucleic Acids Res] 2026 Apr 13; Vol. 54 (7). – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Oxford+University+Press%22">Oxford University Press </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>0411011 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>1362-4962 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2203051048%22">03051048 </searchLink><i>NLM ISO Abbreviation: </i>Nucleic Acids Res <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=41994867 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1093/nar/gkag301 Languages: – Code: eng Text: English Titles: – TitleFull: Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Malecova B – PersonEntity: Name: NameFull: Sala D – PersonEntity: Name: NameFull: Melikian GM – PersonEntity: Name: NameFull: Johns R – PersonEntity: Name: NameFull: Erdogan G – PersonEntity: Name: NameFull: Hartmann M – PersonEntity: Name: NameFull: Jordan M – PersonEntity: Name: NameFull: Arias JD – PersonEntity: Name: NameFull: Bhattacharya A – PersonEntity: Name: NameFull: Meng Q – PersonEntity: Name: NameFull: Dansereau O – PersonEntity: Name: NameFull: Beppler SW – PersonEntity: Name: NameFull: Doppalapudi VR – PersonEntity: Name: NameFull: Huang H – PersonEntity: Name: NameFull: Flanagan WM – PersonEntity: Name: NameFull: Levin AA IsPartOfRelationships: – BibEntity: Dates: – D: 13 M: 04 Text: 2026 Apr 13 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 1362-4962 Numbering: – Type: volume Value: 54 – Type: issue Value: 7 Titles: – TitleFull: Nucleic acids research Type: main |
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