Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD.

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Title: Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD.
Authors: Malecova B; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Sala D; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Melikian GM; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Johns R; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Erdogan G; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Hartmann M; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Jordan M; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Arias JD; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Bhattacharya A; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Meng Q; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Dansereau O; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Beppler SW; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Doppalapudi VR; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Huang H; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Flanagan WM; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA., Levin AA; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.
Source: Nucleic acids research [Nucleic Acids Res] 2026 Apr 13; Vol. 54 (7).
Publication Type: Journal Article
Journal Info: Publisher: Oxford University Press Country of Publication: England NLM ID: 0411011 Publication Model: Print Cited Medium: Internet ISSN: 1362-4962 (Electronic) Linking ISSN: 03051048 NLM ISO Abbreviation: Nucleic Acids Res Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: <searchLink fieldCode="AU" term="%22Malecova+B%22">Malecova B</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Sala+D%22">Sala D</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Melikian+GM%22">Melikian GM</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Johns+R%22">Johns R</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Erdogan+G%22">Erdogan G</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Hartmann+M%22">Hartmann M</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Jordan+M%22">Jordan M</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Arias+JD%22">Arias JD</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Bhattacharya+A%22">Bhattacharya A</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Meng+Q%22">Meng Q</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Dansereau+O%22">Dansereau O</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Beppler+SW%22">Beppler SW</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Doppalapudi+VR%22">Doppalapudi VR</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Huang+H%22">Huang H</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Flanagan+WM%22">Flanagan WM</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.<br /><searchLink fieldCode="AU" term="%22Levin+AA%22">Levin AA</searchLink>; Avidity Biosciences, Inc., 3020 Callan Rd, San Diego, CA 92121, USA.
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              Text: 2026 Apr 13
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