Non-viral gene therapy for hemophilia A: long-term outcomes of minicircle FVIII delivery in a mouse model.
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| Title: | Non-viral gene therapy for hemophilia A: long-term outcomes of minicircle FVIII delivery in a mouse model. |
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| Authors: | Kao YT; Department of Life Sciences, and Doctorial Program in Translational Medicine, National Chung Hsing University, Taichung, Taiwan.; Ph.D. Program in Tissue Engineering and Regenerative Medicine, National Health Research Institutes and National Chung Hsing University, Taichung, Taiwan., Yen CC; Department of Life Sciences, and Doctorial Program in Translational Medicine, National Chung Hsing University, Taichung, Taiwan.; Department of Internal Medicine, China Medical University Hospital, and China Medical University, Taichung, Taiwan., Ro-Lin Chang G; Department of Life Sciences, and Doctorial Program in Translational Medicine, National Chung Hsing University, Taichung, Taiwan., Chiang HT; Department of Life Sciences, and Doctorial Program in Translational Medicine, National Chung Hsing University, Taichung, Taiwan., Chen JK; Ph.D. Program in Tissue Engineering and Regenerative Medicine, National Health Research Institutes and National Chung Hsing University, Taichung, Taiwan.; Institute of Biomedical Engineering and Nanomedicine, National Health Research Institutes, Tainan, Taiwan., Sufian M; Institute of Molecular Biology and Biotechnology (IMBB), The University of Lahore, Lahore, Pakistan., Chen IC; Department of Life Sciences, and Doctorial Program in Translational Medicine, National Chung Hsing University, Taichung, Taiwan., Yang SH; Department of Physiology, Institute of Basic Medical Sciences, National Cheng Kung University, Tainan, Taiwan., Chen CM; Department of Life Sciences, and Doctorial Program in Translational Medicine, National Chung Hsing University, Taichung, Taiwan.; Ph.D. Program in Tissue Engineering and Regenerative Medicine, National Health Research Institutes and National Chung Hsing University, Taichung, Taiwan.; The iEGG and Animal Biotechnology Center, Rong Hsing Research Center for Translational Medicine, National Chung Hsing University, Taichung, Taiwan.; Center for General Educational, National Quemoy University, Kinmen, Taiwan. |
| Source: | Frontiers in pharmacology [Front Pharmacol] 2026 Apr 09; Vol. 17, pp. 1742144. Date of Electronic Publication: 2026 Apr 09 (Print Publication: 2026). |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Frontiers Media] Country of Publication: Switzerland NLM ID: 101548923 Publication Model: eCollection Cited Medium: Print ISSN: 1663-9812 (Print) Linking ISSN: 16639812 NLM ISO Abbreviation: Front Pharmacol Subsets: PubMed not MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 1663-9812 |
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| DOI: | 10.3389/fphar.2026.1742144 |