First-Generation TTR Silencing Therapies in Hereditary Transthyretin Amyloidosis With Polyneuropathy: Real-World Insights From a German Single-Referral Center.

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Title: First-Generation TTR Silencing Therapies in Hereditary Transthyretin Amyloidosis With Polyneuropathy: Real-World Insights From a German Single-Referral Center.
Authors: Koch MS; Amyloidosis Center, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.; Department of Neurology, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany., Siepen FAD; Amyloidosis Center, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.; Department of Cardiology, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany., Hegenbart U; Amyloidosis Center, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.; Department of Medicine V, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany., Schönland S; Amyloidosis Center, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.; Department of Medicine V, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany., Weiler M; Amyloidosis Center, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.; Department of Neurology, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.
Source: European journal of neurology [Eur J Neurol] 2026 Feb; Vol. 33 (2), pp. e70529.
Publication Type: Journal Article
Journal Info: Publisher: Wiley Country of Publication: England NLM ID: 9506311 Publication Model: Print Cited Medium: Internet ISSN: 1468-1331 (Electronic) Linking ISSN: 13515101 NLM ISO Abbreviation: Eur J Neurol Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:1468-1331
DOI:10.1111/ene.70529