First-Generation TTR Silencing Therapies in Hereditary Transthyretin Amyloidosis With Polyneuropathy: Real-World Insights From a German Single-Referral Center.
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| Title: | First-Generation TTR Silencing Therapies in Hereditary Transthyretin Amyloidosis With Polyneuropathy: Real-World Insights From a German Single-Referral Center. |
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| Authors: | Koch MS; Amyloidosis Center, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.; Department of Neurology, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany., Siepen FAD; Amyloidosis Center, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.; Department of Cardiology, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany., Hegenbart U; Amyloidosis Center, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.; Department of Medicine V, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany., Schönland S; Amyloidosis Center, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.; Department of Medicine V, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany., Weiler M; Amyloidosis Center, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany.; Department of Neurology, Heidelberg University Hospital, and Faculty of Medicine, Heidelberg University, Heidelberg, Germany. |
| Source: | European journal of neurology [Eur J Neurol] 2026 Feb; Vol. 33 (2), pp. e70529. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Wiley Country of Publication: England NLM ID: 9506311 Publication Model: Print Cited Medium: Internet ISSN: 1468-1331 (Electronic) Linking ISSN: 13515101 NLM ISO Abbreviation: Eur J Neurol Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 1468-1331 |
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| DOI: | 10.1111/ene.70529 |